Youn Bok Lee

Gene therapy is a powerful and innovative approach for patients using molecular biology tools to engineer genetic materials. Our team is developing gene therapy trials for FTD/ALS and the multiple types of gene therapy vectors and delivery strategies. We are also involved in the regulatory and operational challenges associated with gene therapy trials, including early discovery, vector science, pre-clinical studies and CMC (chemistry, manufacturing and controls). We have a strong Industry partnership with King’s College London spinout company AviadoBio. As I am a co-founder of the AviadoBio (vice president and Head of discovery), our lab is developing transformative medicines with an industry partner for patients living with debilitating and life-threatening neurodegenerative disorders.